The global Phenylketonuria Treatment Market Growth Accelerated by Increasing Research and Development Activities


 Phenylketonuria (PKU) is a rare genetic disease that prevents the body from breaking down phenylalanine properly. Left untreated, PKU can cause intellectual disabilities, seizures, behavioral problems and other lifelong disabilities. Treatment for PKU includes following a strict low-protein diet along with medications. Advances in PKU treatment options have improved the management and quality of life for patients. The global Phenylketonuria Treatment Market is estimated to be valued at US$ 1 Bn in 2023 and is expected to exhibit a CAGR of 8.6% over the forecast period 2023 to 2030, as highlighted in a new report published by Coherent Market Insights.


Market key trends:

One of the key trends driving the growth of the phenylketonuria treatment market is increasing research and development activities for developing novel drugs and treatment procedures. PKU can cause lifelong disabilities if left untreated. Therefore, several pharmaceutical and biotech companies are focusing on developing new drugs that can eliminate the need to follow a strict low-protein diet or lessen its dependency. For instance, BioMarin Pharmaceuticals is developing a gene therapy named valoctocogene roxaparvovec for treating PKU. If approved, it will be the first gene therapy available for PKU that can potentially eliminate the need for the lifelong low-protein diet. Such ongoing R&D activities for developing transformative therapies are expected to fuel the growth of this market over the forecast period.
Segment Analysis
The global phenylketonuria treatment market is dominated by the dietary management segment. Dietary management focuses on maintaining low levels of phenylalanine in the blood through the intake of a special low-phenylalanine diet. It is considered the primary form of treatment for phenylketonuria. The diet aims to prevent intellectual disability by restricting phenylalanine intake. Compliance to the diet is therefore critical to avoidance of long-term neurological complications.

Key Takeaways
The global phenylketonuria treatment market is expected to witness high growth over the forecast period driven by rising incidence of phenylketonuria and increasing adoption of pioneering treatments.

Regional analysis: North America currently dominates the global phenylketonuria treatment market and is expected to continue its dominance over the forecast period. This is attributed to high awareness about PKU, availability of advanced treatment options, and favorable reimbursement policies in the region. Asia Pacific is anticipated to emerge as the fastest growing regional market driven by improving healthcare infrastructure and increasing healthcare expenditure in countries like China and India.

Key players: Key players operating in the phenylketonuria treatment market are BioMarin Pharmaceuticals Inc., Censa Pharmaceutical, Synlogic Inc., Erytech Pharma SA, Codexis Inc., SOM Innovation Biotech SL, Homology Medicines Inc., and Ultragenyx (Dimension Therapeutics). BioMarin Pharmaceuticals dominates with its flagship medication Palynziq (pegvaliase-pqpz) injection used for the treatment of phenylketonuria in adult patients.

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